Results from Genentech s Evrysdi Study in Infants with Type 1 SMA Published in NEJM
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Roche announces results from Evrysdi (risdiplam) study in infants with Type 1 spinal muscular atrophy (SMA) published in New England Journal of Medicine
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Positive Data from FIREFISH Study of Evrysdi™ (risdiplam) in Infants with Type 1 Spinal Muscular Atrophy Published in The New England Journal of Medicine Results found that patients treated with Evrysdi at 12 months demonstrated significant improvements in survival and developmental milestones The U.S. Food and Drug Administration approved Evrysdi in August 2020 as the first and only at home SMA treatment with proven efficacy in adults, children and infants 2 months and older
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SOUTH PLAINFIELD, N.J., Feb. 24, 2021 /PRNewswire/ PTC Therapeutics, Inc. (NASDAQ: PTCT), today announced the publication of results from the dose finding Part 1 of the pivotal FIREFISH study evaluating Evrysdi™ (risdiplam) in infants with symptomatic type 1 spinal muscular atrophy (SMA) in The New England Journal of Medicine (NEJM)
Study looks at six-and-a-half year olds given experimental formula up to six months of age A recent study published in the American Journal of Clinical Nutrition looked at the neurodevelopment and growth of to the age of six-and-a-half who consumed a low-energy, low-protein formula supplemented with bovine milk fat globule membranes.
The researchers previously reported results from a randomized controlled trial in which they found Swedish infants consuming an experimental low-energy, low-protein formula (EF) supplemented with bovine milk fat globule membranes (MFGMs) up to six months of age had several positive outcomes, including better performance in the cognitive domain of Bayley Scales of Infant and Toddler Development 3rd Edition at 12 months of age, and higher plasma cholesterol concentrations during the intervention, than infants consuming standard formula (SF).