/PRNewswire/ The iron overload disorder hereditary hemochromatosis is the most common genetic disorder in the Caucasian population. If untreated, iron.
/PRNewswire/ OxThera AB, a privately-held biopharmaceutical company dedicated to improving the lives of people with Primary Hyperoxaluria (PH), announces.
/PRNewswire/ Mucopolysaccharidosis type I Hurler (MPS-IH) is caused by a deficiency in alpha-L-iduronidase (IDUA) and is typically managed by allogeneic.