MSNBC The Rachel Maddow Show August 30, 2019 01:46:00
University of california has a good children's hospital. when isabel was 7 years old she was invited to come to that facility for treatment. isabel had been born with a rare genetic disease called mps 6. it means that her body is lacking an enzyme that she needs for all sorts of things. it causes severe damage for her body and her cells that won't get better. ucsf wanted to launch an important clinical trial to launch a treatment. they needed her to be in the trial to do it. rare is an important word in this story, right? her rare disease. by definition, for any rare disease there just aren't ...