Best Practices For Designing And Running Clinical Trials For Patients With Rare Diseases
Best Practices For Designing And Running Clinical Trials For Patients With Rare Diseases By L. Mary Smith, Ph.D., SpringWorks Therapeutics Most people agree that drug development is risky and challenging, and as an industry, we are constantly searching for ways to improve the drug development process – particularly in the rare disease space. SpringWorks Therapeutics works hard to develop patient-centric clinical trials for rare diseases and has found success through fostering collaborative partnerships with patient advocacy organizations and allowing for new flexibilities in trial design....