Lysogene Provides Additional Update on AAVance Phase 2/3 Gene Therapy Clinical Trial with LYS-SAF302 in children with MPS IIIA
Positive biomarker data confirmed in additional subjects and at additional timepoints Stable or continuously increasing cognitive, language and motor functions observed in patients treated
United States Raymond Wang Foundation Of Caring Multidisciplinary Lysosomal Disorder Program Sanfilippo Community Conference Weizmann Institute Of Science Bayley Scales Of Infant Development
Source: finanznachrichten.de