vimarsana.com

Latest Breaking News On - Leen thielemans - Page 1 : vimarsana.com

Antisense Oligonucleotide Fast Tracked for Myotubular and Centronuclear Myopathies

DYN101 receives Fast Track designation for the treatment of myotubular and centronuclear myopathies.

Dynacure Receives Fast Track Designation for DYN101, an Investigational Antisense Oligonucleotide for the Treatment of Myotubular and Centronuclear Myopathies

Dynacure Receives Fast Track Designation for DYN101, an Investigational Antisense Oligonucleotide for the Treatment of Myotubular and Centronuclear Myopathies

/PRNewswire/ Dynacure, a clinical stage biotechnology company focusing on Myotubular and Centronuclear Myopathies (CNM), a group of rare, debilitating, and.

Dynacure Announces FDA Acceptance of Investigational New Drug Application for DYN101 for Myotubular and Centronuclear Myopathies

Dynacure announces publication of Hierarchical Bayesian modelling of disease progression in Orphanet Journal of Rare Diseases

Dynacure announces publication of Hierarchical Bayesian modelling of disease progression in Orphanet Journal of Rare Diseases Bayesian statistical approach based on natural history study could address clinical trial design challenges in centronuclear myopathy News provided by Share this article Share this article STRASBOURG, France and PHILADELPHIA, Jan. 15, 2021 /PRNewswire/  Dynacure, a clinical-stage company focused on developing and commercializing novel therapies to transform the lives of patients with rare diseases who have limited or no treatment options, announced the publication of a paper entitled, Hierarchical Bayesian modelling of disease progression to inform clinical trial design in centronuclear myopathy (CNM). The paper was published this month in Orphanet Journal of Rare Diseases, a scientific, peer-reviewed publication and can be accessed here.

© 2025 Vimarsana

vimarsana © 2020. All Rights Reserved.