Ol Ii News Today

Britain's health regulator said on Wednesday it had revoked a conditional marketing authorisation for Novartis' sickle cell disease drug, Adakveo.

Patients with severe sickle cell disease could soon be freed from vaso-occlusive crises after receiving an infusion of exa-cel, the first gene-editing therapy to use CRISPR technology.

Bluebird bio said on Thursday a large insurer had agreed to cover its newly approved sickle cell disease gene therapy, easing some investor worries about resistance from...

The average age of death for Black US patients with sickle cell disease rose from 39 years in 1999-2009 to 43 years in 2010-2020, reflecting improvements in treatment.

The drug targets a mast cell mutation that gives rise to indolent systemic mastocytosis, a rare and debilitating blood disorder.

Patients who received lovo-cel had durable remissions and reductions in vaso-occlusive events, pain crises, and hospitalizations in the longest running gene therapy trial for sickle cell disease.

The approval for the two gene-editing treatments, called exa-cel and lovo-cel, could help thousands with the blood disorder.

Previously thought to be age-dependent, retinopathy affects a full third of children with sickle cell disease, a new study found.

Lower risk of bacteremia in children with sickle cell disease (SCD) presenting to the emergency department (ED) with fever calls critical reexamination of long standing approach towards management of SCD in children.

When Baltimore internist and AMA trustee Willarda Edwards ran for AMA president, the organization accused her of vote trading. She has sued for defamation and conspiracy.