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Pfizer Provides Update on Phase 3 Study of Investigational Gene Therapy for Ambulatory Boys with Duchenne Muscular Dystrophy

Pfizer Inc. today announced that CIFFREO, a Phase 3 global, multicenter, randomized, double-blind, placebo-controlled study evaluating the investigational mini-dystrophin gene therapy,.

Dan levyFordadistrogene movaparvovec clinical programPfizer incExchange commissionDevelopment head for duchenneNorth star ambulatory assessmentDevelopment headFordadistrogene movaparvovec clinicalBreakthroughs that change patientPfizer newsAnnual reportLooking informationFactors that may affect futureOrphanetj rare

Pfizer Provides Update on Phase 3 Study of Investigational Gene Therapy for Ambulatory Boys with Duchenne Muscular Dystrophy

NEW YORK (BUSINESS WIRE) Jun 12, 2024

Dan levyPfizer incDevelopment head for duchenneExchange commissionFordadistrogene movaparvovec clinical programNorth star ambulatory assessmentDevelopment headFordadistrogene movaparvovec clinicalBreakthroughs that change patientPfizer newsAnnual reportLooking informationFactors that may affect futureOrphanetj rareBusiness wire

SpringWorks Therapeutics Announces Data to be Presented at the 2024 American Society of Clinical Oncology (ASCO) Annual Meeting

SpringWorks Therapeutics Announces Data to be Presented at the 2024 American Society of Clinical Oncology (ASCO) Annual Meeting
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United statesSamantha hilson sandlerChristopherl moertelBetty jayne dahlbergJim cassidyUniversity of minnesota school medicineClinical research divisionAmerican society of clinical oncologyFred hutchinson cancer centerChildren tumor foundationEuropean medicines agencyHealth supervision for children with neurofibromatosis typeNeurofibromatosis programDrug administrationSpringworks therapeutics incDesmoid tumor working group

SpringWorks Therapeutics Announces Data to be Presented at the 2024 American Society of

– Results from pivotal Phase 2b ReNeu trialofmirdametinib in patients with NF1-PN to be presented in an oral presentation –

United statesChristopherl moertelBetty jayne dahlbergJim cassidySamantha hilson sandlerUniversity of washingtonChildren tumor foundationNeurofibromatosis programFred hutchinson cancer centerHealth supervision for children with neurofibromatosis typeEuropean commissionClinical research divisionSpringworks therapeutics incEuropean medicines agencyUs department of commerceAmerican society of clinical oncology

SpringWorks Therapeutics Announces Abstracts Accepted for Presentation at the 2024 American

– Results from Phase 2b ReNeu trial of mirdametinib in NF1-PN accepted for oral presentation –

United statesBruno vincenziJim cassidyBernd kasperSamantha hilson sandlerChristopher moertelHealth supervision for children with neurofibromatosis typeDesmoid tumor working groupEuropean medicines agencyDrug administrationUs department of commerceSpringworks therapeutics incChildren tumor foundationAmerican society of clinical oncologyEuropean commissionWorks therapeutics