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Eplontersen granted U.S. FDA Fast Track designation for patients with transthyretin-mediated amyloid cardiomyopathy

CARLSBAD, Calif., Feb. 8, 2024 /PRNewswire/ -- Ionis Pharmaceuticals, Inc. announced today that the U.S. Food and Drug Administration has granted Fast Track designation to Ionis and AstraZenecas...
Sarah Walters Eugene Schneider Ionis Pharmaceuticals Drug Administration Ionis Pharmaceuticals Inc Columbia University Irving Medical Center

Ionis poised for continued momentum in 2024 with product launches and key advances in robust pipeline of investigational medicines for serious diseases

– Numerous value-driving commercial, regulatory and pipeline milestones anticipated – CARLSBAD, Calif., Jan. 8, 2024 /PRNewswire/ -- Ionis Pharmaceuticals, Inc. today announced highlights from...
European Medicines Agency Drug Administration Ionis Pharmaceuticals Ionis Pharmaceuticals Inc Healthcare Conference Highlights Include

WAINUA™ (eplontersen) granted regulatory approval in the U.S. for the treatment of adults with polyneuropathy of hereditary transthyretin-mediated amyloidosis

/PRNewswire/ -- Ionis Pharmaceuticals, Inc. (Nasdaq: IONS) announced today that the U.S. Food and Drug Administration (FDA) has approved Ionis and...
United States Michaelj Polydefkis Isabelle Lousada Journal Of The American Medical Association Ionis Pharmaceuticals Prnewswire Ionis Pharmaceuticals Inc

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Alnylam Presents 18-Month Results from the APOLLO-B Phase 3 Study of Patisiran in Patients with ATTR Amyloidosis with Cardiomyopathy

– Continued Treatment with Patisiran in Open-Label Extension Period Showed Evidence of Sustained Benefit across Measures of Functional Capacity and Health Status and Quality of Life, as well as... | May 20, 2023
United States United Kingdom Renan Denoncourt European Union Alnylam Pharmaceuticals Alnylam Pharmaceuticals Nasdaq

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