Despite Risk, Patients With SCD Hopeful About Gene Therapies
Sickle cell disease (SCD) has known complications that include organ damage and failure, rhabdomyolysis, glaucoma, splenic sequestration, and vaso-occlusive crises. At present, the only potential cure is a bone marrow transplant, but it can be difficult to find a donor and there is a high rejection risk.
United States Juan Marcos Gonzalez American Society Of Hematology University Of North Carolina At Chapel Hill Duke University Health System African American
Source: ajmc.com