Innovative neurosurgical technique used in Tay-Sachs gene therapy clinical trial By Susan E.W. Spencer March 03, 2021
When the first patient in a new clinical trial was given a gene therapy targeting infantile Tay-Sachs and Sandhoff diseases in January, an innovative procedure that represents a “new frontier for neurosurgery” was used to deliver the therapeutic.
Red arrows indicate the location
in the thalamus where the
infusion is targeted.
The trial, by Sio Gene Therapies (formerly known as Axovant), is an open-label, two-stage, clinical study designed to evaluate safety and dose-escalation and safety and efficacy of surgical delivery of AXO-AAV-GM2 to the brain and spinal cord of trial participants with infantile or juvenile GM2 gangliosidosis. Sio licensed exclusive worldwide rights from UMass Medical School for the development and commercialization of gene therapy programs for GM1 gangliosidosis and GM2 gangliosidosis, including
Vet Set Go and Merck Animal Health Team Up to Launch the “Become a Veterinarian Camp Contest 2021”
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Contest Gives 6th – 8th Graders the Chance to Win a Coveted Spot at the Virtual Auburn University College of Veterinary Medicine Junior Vet Camp from July 13-15, 2021; Online essay contest opens Monday, March 1, at 8:00 a.m. EST; Entries due Wednesday, March 31, at 11:59 p.m. EST
Vet Set Go is the first and only web community dedicated to helping teen and tween aspiring veterinarians explore their passion.
During the camp, contest winners will learn about veterinary medicine in Auburn University classrooms, laboratories, and outdoor facilities.
First patient dosed in clinical trial of gene therapy for Tay-Sachs and Sandhoff disease umassmed.edu - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from umassmed.edu Daily Mail and Mail on Sunday newspapers.
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The American Association of Equine Practitioners (AAEP) announced incoming officials and recognized its 2020 award winners Dec. 6-9 during the 2020 Annual Convention & Trade Show, held virtually. New officials included:
President: Scott Hay, DVM, president and managing shareholder of Fort Lauderdale, Florida-based racetrack practice Teigland, Franklin and Brokken DVMs
Vice president: Rob Franklin, DVM, Dipl. ACVIM, partner in Fredericksburg Equine Veterinary Services in Fredericksburg, Texas, and a founding director of the Equitarian Initiative
Treasurer: Amy Grice, VMD, MBA, a veterinary business consultant in Virginia City, Montana
Board of directors: Emma Adam, DVM, PhD, Dipl. ACVIM, ACVS, an equine outreach veterinarian for the University of Kentucky Department of Veterinary Science, in Lexington