Parent Project Muscular Dystrophy Awards $450,000 to Collaborative Duchenne Muscular Dystrophy Care Projects
2021 Certified Duchenne Care Center Inter-Institutional Collaboration Grant Program Supports Three Projects Addressing Gaps in Care
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HACKENSACK, N.J., April 6, 2021 /PRNewswire/ Parent Project Muscular Dystrophy (PPMD), a nonprofit organization leading the fight to end Duchenne muscular dystrophy (Duchenne) is pleased to announce awards to three collaborative Certified Duchenne Care Center (CDCC) network projects totaling $450,000. Under the organization s 2021 CDCC Inter-Institutional Collaboration Grant Program, these grants will support the work of twenty centers from across the country working together to address a universal quality improvement or care need that can be advanced by collaborative guidance and training.
Nationwide Children s/Andelyn gene therapy facility to open in Columbus in 2022
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UVA researcher developing innovative gene therapy to help children with Rett syndrome
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Scientist at UVA School of Medicine developing gene therapy to help with Rett syndrome A scientist at the UVA School of Medicine is developing a gene therapy for Rett syndrome. By Daniel Grimes | March 15, 2021 at 6:22 PM EDT - Updated March 15 at 8:46 PM
CHARLOTTESVILLE, Va. (WVIR) - A scientist at the University of Virginia School of Medicine is developing a gene therapy that could help young girls across the country suffering from Rett syndrome.
Rett syndrome is caused by a mutation on the X chromosome. It affects brain development, which can lead to seizures and breathing problems.
Sanchita Bhatnagar is partnering with a scientist at the Center for Gene Therapy to bring about change for those living with Rett syndrome. They aim to manipulate cell regulators to only express healthy copies of certain proteins called microRNA’s.
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(COLUMBUS, Ohio) - High-powered magnets are small, shiny magnets made from powerful rare earth metals. Since they started showing up in children s toys in the early 2000s and then later in desk sets in 2009, high-powered magnets have caused thousands of injuries and are considered to be among the most dangerous ingestion hazards in children.
When more than one is swallowed, these high-powered magnets attract to each other across tissue, cutting off blood supply to the bowel and causing obstructions, tissue necrosis, sepsis and even death. The U.S. Consumer Product Safety Commission (CPSC) found them dangerous enough that in 2012 they halted the sale of high-powered magnet sets and instituted a recall followed by a federal rule that effectively eliminated the sale of these products. This rule was overturned by the U.S. Court of Appeals in December 2016.