PTC Presents Results from a Real-World Study of Steroid Swit

PTC Presents Results from a Real-World Study of Steroid Switching in the Treatment of Patients with Dystrophinopathies

PTC Therapeutics, Inc. (NASDAQ: PTCT) today announced results from a real-world study of patients with Duchenne muscular dystrophy (DMD) and Becker muscular dystrophy (BMD) who switched from prednisone to EMFLAZA® (deflazacort) following the FDA approval. The primary reason the majority of patients chose to switch to EMFLAZA was a desire to delay disease progression to improve the benefit and tolerability. During the 6-months average follow-up after switching, physician-reported outcomes were consistent with EMFLAZA addressing the primary reasons for switching. Data were presented at the 2021 Muscular Dystrophy Association (MDA) Virtual Clinical and Scientific Conference.

Related Keywords

, Duchenne Muscular Dystrophy , Ptc Therapeutics , Muscular Dystrophy Association , Slow Disease Progression , Corticosteroids , Becker Muscular Dystrophy , Muscular Dystrophy , Prednisone , ட சிகிச்சை , தசை டிஸ்ட்ரோபி சங்கம் , மெதுவாக நோய் ப்ரோக்ரெஶந் , பெக்கர் தசை டிஸ்ட்ரோபி , தசை டிஸ்ட்ரோபி ,

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