BBCNEWS BBC News at One June 4, 2024 12:14:00
By using a harmless virus, like a post—van, really, to deliver the gene to the liver which was then able to use the correct instructions to make the protein. this has helped these people, but the question is, scientists will have to look at larger trials to see if it works for more people. they also have to consider costs because gene therapy is expensive, and of course the side effects as well. the hope is that this trial and lots of other trials into genetic therapies for haemophilia will transform the lives of people with the most severe haemophilia in uk.— of people with the most sever...