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FDA OKs Vutrisiran for hATTR Amyloidosis With Polyneuropathy : vimarsana.com
FDA OKs Vutrisiran for hATTR Amyloidosis With Polyneuropathy
Vutrisiran, an RNAi therapeutic given by subcutaneous injection once every 3 months, significantly improved signs and symptoms of hATTR polyneuropathy in a phase 3 study.
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