Spinraza Nusinersen News Today

SMN-based gene therapy has offered many patients with SMA and their families hope for a better future. Dr Sheetal Sharda, clinical geneticist and director of genomics division, Neuberg Centre for Genomic Medicine (NCGM) reveals more

Diagnosed with a rare neuromuscular disorder, 25-year-old Marina Lisovaya needs a costly treatment to stop her condition from getting worse and save her from dying young.

Diagnosed with a rare neuromuscular disorder, 25-year-old Marina Lisovaya needs a costly treatment to stop her condition from getting worse and save her from dying young.