Contributor: How Patients and Caregivers Can Be a Catalyst f

Patient input and experiences play a crucial role in advancing rare disease research and therapy development, as they help define the disease, inform clinical trial design, and influence regulators and payers' decisions, ultimately serving as catalysts for innovation in the field.

Related Keywords

United States , Milan , Lombardia , Italy , Kyle Bryant , Philip Cyr , Nguengang Wakap , International Meeting , Drug Administration , Friedreich Ataxia Research Alliance , Agency For Healthcare Research , Youtube , Ataxia Research Alliance , Orphan Drug Act , Drug Evaluation , Innov Regul , Annual International , Annual European Meeting , Accessed September , Evaluating Patient Outcomes , Healthcare Research , Rare Disease , Future Rare , Health Access ,