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The FDA has granted Breakthrough Therapy designation to diazoxide choline for the treatment of adults and children ages 4 years and older with genetically confirmed Prader-Willi syndrome (PWS) who have hyperphagia.
FOSTER CITY, Calif.--(BUSINESS WIRE)--May 18, 2024--
- Seven abstracts highlighting ALGS and PFIC data, including three oral presentations - Long-term extension data from Phase 3 MARCH-ON PFIC study presented at plenary session and selected among the...
The Data Monitoring Committee recommended to continue the clinical trial without modification of the current protocol, based on the pre-planned review of safety data.The recommendation was based on...
ZUG, Switzerland--(BUSINESS WIRE)--May 7, 2024--