Rare Disease Program News Today : Breaking News, Live Updates & Top Stories | Vimarsana

The Walk to Make Cystic Fibrosis History had a big day in its 9th edition raising almost $40,000.

16.03.2023 - - NUZYRA (omadacycline) Generated Net U.S. Sales of $98.7 Million from the Core Commercial Business, a 45% Increase Over the Prior Year - Continued Progress on the Rare Disease Nontuberculous Mycobacteria (NTM) & BARDA Project BioShield Anthrax ...

Capital Region parents push for FDA reform of rare disease drug reviews Federal legislation would require rare disease experts, patients weigh in when drugs come up for review FacebookTwitterEmail U.S. Rep. Paul Tonko, D-NY, holds a virtual discussion on legislation he says would strengthen the FDA review process for approving rare disease treatments.Screenshot Capital Region parents are helping lead the push for bipartisan federal legislation that advocates say would lead to better, easier and more affordable treatment for rare diseases. The parents, all of whom have children in the area wit...