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CRISPR-Based Gene Therapy Earns Beta Thalassemia Approval

Exa-cel earned its second FDA approval. The one-time therapy, which has a list price of $2.2 million in the United States, should be available for patients early this year.

United-states , Drug-administration , Vertex-pharmaceutical , Genomics-genomic-medicine , Beta-thalassemia , Crispr , Lustered-regularly-interspaced-short-palindromic-repeats , Rispr-cas9 , Thalassemia-thalassaemia , Biologic-therapy , Iologics