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First Observational Study Initiated in Sanfilippo Syndrome T
First Observational Study Initiated in Sanfilippo Syndrome T
First Observational Study Initiated in Sanfilippo Syndrome Type D
Potential lead-in trial to drug trial of novel enzyme replacement therapy Phoenix Nest Logo BROOKLYN, N.Y. - January 10, 2023 - (Newswire.com)...
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