Sickle-Cell Treatment Created With Gene Editing Wins U.K. Approval
The first treatment that relies on CRISPR is expected to receive U.S. approval next month. But it may cost millions of dollars per patient.
Stay updated with breaking news from Crispr. Get real-time updates on events, politics, business, and more. Visit us for reliable news and exclusive interviews.
The first treatment that relies on CRISPR is expected to receive U.S. approval next month. But it may cost millions of dollars per patient.
Initial data from a human clinical trial suggests an experimental drug from Verve Therapeutics that uses gene editing to permanently lower cholesterol raises hopes that people can one day trade daily lipid-lowering pills for a one-time treatment
It’s still early days for a novel form of gene therapy called base editing, but this small study in people with extremely high cholesterol shows striking results.
A small trial of a cholesterol-lowering treatment based on CRISPR gene editing has produced promising results, but there are questions over safety
New therapies are on the horizon for genetic neuromuscular diseases, and this will raise both hopes for patients and challenges for neurologists.