Spinraza benefits SMA children not helped by Zolgensma: Interim data smanewstoday.com - get the latest breaking news, showbiz & celebrity photos, sport news & rumours, viral videos and top stories from smanewstoday.com Daily Mail and Mail on Sunday newspapers.
Data from ongoing FIREFISH study confirm long-term efficacy and safety profile of Evrysdi in children with Type 1 SMANinety-one percent of children were.
– Data from ongoing FIREFISH study confirm long-term efficacy and safety profile of Evrysdi in children with Type 1 SMA –
– Ninety-one percent of children were alive at month 48 –
– More than 95% maintained the ability to swallow - without treatment they would have required feeding support and majority would have died within 2 years –
– Evrysdi is now approved in 99 countries with more than 8,500 patients treated globally –