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Alnylam Reports Updated Positive Interim Phase 1 Results for ALN-APP, in Development for Alzheimer's Disease and Cerebral Amyloid Angiopathy

– First Clinical Study of a Central Nervous System-Administered RNAi Therapeutic Showed Rapid and Robust Target Engagement with Sustained Effect Over 6 Months with a Single Dose –


– ALN-APP Continues to Demonstrate an Encouraging Clinical Safety and Tolerability Profile –


– Multiple-dose Portion of Study, Part B, Being Initiated in Approved Regions – ....

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Alnylam presents promising results for RNAi therapeutic in Alzheimer's disease at AAIC

Alnylam presents promising results for RNAi therapeutic in Alzheimer's disease at AAIC
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