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Precision BioSciences Announces Receipt of FDA Fast Track Designation for ECUR-506, iECURE's Program for the Treatment of Neonatal Onset Ornithine Transcarbamylase (OTC) Deficiency

Precision BioSciences Announces Receipt of FDA Fast Track Designation for ECUR-506, iECURE's Program for the Treatment of Neonatal Onset Ornithine Transcarbamylase (OTC) Deficiency
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Ultragenyx Reports First Quarter 2024 Financial Results and Corporate Update

First quarter total revenue of $109 million, Crysvita® revenue of $83 million and Dojolvi® revenue of $16 million Reaffirmed 2024 expected total revenue guidance between $500 million to $530. ....

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Ultragenyx Earnings: No Visible Path To Financial Success Yet (NASDAQ:RARE)

Ultragenyx Earnings: No Visible Path To Financial Success Yet (NASDAQ:RARE)
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Ultragenyx Reports Fourth Quarter and Full Year 2023 Financial Results and Corporate Update

2023 Total Revenue of $434 million, Crysvita® revenue of $328 million and Dojolvi® revenue of $71 million 2024 Financial Guidance: Total Revenue between $500 million and $530 million, Crysvita. ....

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Ultragenyx Reports Fourth Quarter and Full Year 2023 Financial Results and Corporate Update

Ultragenyx Reports Fourth Quarter and Full Year 2023 Financial Results and Corporate Update
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