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Appendix 4c Quarterly Activity Report for Quarter Ended March 31, 2024

Appendix 4c Quarterly Activity Report for Quarter Ended March 31, 2024
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SpringWorks Therapeutics Announces Abstracts Accepted for Presentation at the 2024 American Society of Clinical Oncology (ASCO) Annual Meeting

SpringWorks Therapeutics Announces Abstracts Accepted for Presentation at the 2024 American Society of Clinical Oncology (ASCO) Annual Meeting
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SpringWorks Therapeutics Announces Abstracts Accepted for Presentation at the 2024 American ...

– Results from Phase 2b ReNeu trial of mirdametinib in NF1-PN accepted for oral presentation –

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SpringWorks Therapeutics Announces Abstracts Accepted for Presentation at the 2024 American Society of Clinical Oncology (ASCO) Annual Meeting

SpringWorks Therapeutics Announces Abstracts Accepted for Presentation at the 2024 American Society of Clinical Oncology (ASCO) Annual Meeting
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Day One's OJEMDA™ (tovorafenib) Receives US FDA Accelerated Approval for Relapsed or Refractory BRAF-altered Pediatric Low-Grade Glioma (pLGG), the Most Common Form of Childhood Brain Tumor

First and only FDA-approved type II RAF inhibitor for patients with relapsed or refractory pLGG harboring a BRAF fusion or rearrangement, or BRAF V600 mutation RAPNO LGG overall response...

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Day One's OJEMDA™ (tovorafenib) Receives US FDA Accelerated

Day One’s OJEMDA™ (tovorafenib) Receives US FDA Accelerated Approval for Relapsed or Refractory BRAF-altered Pediatric Low-Grade Glioma (pLGG), the Most...

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Day One's OJEMDA™ (tovorafenib) Receives US FDA Accelerated Approval for Relapsed or Refractory ... | Region

First and only FDA-approved type II RAF inhibitor for patients with relapsed or refractory pLGG harboring a BRAF fusion or rearrangement, or BRAF V600 mutation

Canada , Australia , California , United-states , Brisbane , Queensland , Laura-cooper , Sabine-mueller , Jeremy-bender , Courtney-davies , Samuel-blackman , Drug-administration

Day One's OJEMDA™ (tovorafenib) Receives US FDA Accelerated Approval for Relapsed or Refractory BRAF-altered Pediatric Low-Grade Glioma (pLGG), the Most Common Form of Childhood Brain Tumor

First and only FDA-approved type II RAF inhibitor for patients with relapsed or refractory pLGG harboring a BRAF fusion or rearrangement, or BRAF V600 mutation RAPNO LGG overall response...

Australia , Brisbane , Queensland , California , United-states , Canada , Jeremy-bender , Sabine-mueller , Laura-cooper , Courtney-davies , Samuel-blackman , European-commission

Day One's OJEMDA™ (tovorafenib) Receives US FDA Accelerated Approval for Relapsed or Refractory BRAF-altered Pediatric Low-Grade Glioma (pLGG), the Most Common Form of Childhood Brain Tumor

Day One's OJEMDA™ (tovorafenib) Receives US FDA Accelerated Approval for Relapsed or Refractory BRAF-altered Pediatric Low-Grade Glioma (pLGG), the Most Common Form of Childhood Brain Tumor
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Belite Bio : Initiates Stargardt Disease Clinical Trial in Japan

Belite Bio Initiates Stargardt Disease Clinical Trial in Japan

April 22, 2024

Tinlarebant is Belite Bio's orally administered tablet...

Japan , Phoenix , Arizona , United-states , Japanese , Belite-bio , Belite-bio-inc , Stargardt-disease , Geographic-atrophy , Dry-age-related-macular-degeneration , Orphan-drug-designation