SMA in Adults: Interim Data Back Nusinersen Efficacy
New trial focuses on drug's performance in spinal muscular atrophy beyond childhood
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New trial focuses on drug's performance in spinal muscular atrophy beyond childhood
20.03.2023 - Genentech, a member of the Roche Group (SIX: RO, ROG; OTCQX: RHHBY), today announced new long-term data for Evrysdi (risdiplam) in a broad range of people aged 2-25 years with spinal muscular atrophy (SMA) from the pivotal SUNFISH study. Data ... Seite 1
Data from pivotal SUNFISH study showed increases in motor function observed during the first year were maintained through the fourth year, while the overall rate of adverse events continued to decrease
CAMBRIDGE, Mass.--(BUSINESS WIRE)--Scholar Rock (NASDAQ: SRRK), a Phase 3 clinical-stage biopharmaceutical company focused on the treatment of serious diseases in which protein growth factors play
Treatment with nusinersen may decrease disease progression in pediatric patients who are nonambulatory with spinal muscular atrophy types 2 and 3.